Measuring patient experiences in Fabry disease: validation of the Fabry-specific Pediatric Health and Pain Questionnaire (FPHPQ)
Ramaswami Uma, Stull, Parini Rossella, Pintos-Morell Guillem, Whybra Catharina, Kalkum Gisela, Rohrbach Marianne, Raluy-Callado Mireia, Beck Michael, Chen Wen-Hung, Wiklund Ingela, On